| An ex vivo gene therapy approach to treat muscular dystrophy using inducible pluripotent stem cells A Filareto, S Parker, R Darabi, L Borges, M Iacovino, T Schaaf, ... Nature communications 4 (1), 1549, 2013 | 160 | 2013 |
| Assessment of the Myogenic Stem Cell Compartment Following Transplantation of Pax3/Pax7-Induced Embryonic Stem Cell-Derived Progenitors R Darabi, FNC Santos, A Filareto, W Pan, R Koene, MA Rudnicki, M Kyba, ... Stem cells 29 (5), 777-790, 2011 | 141 | 2011 |
| In Vivo and In Vitro Studies Support That a New Splicing Isoform of OLR1 Gene Is Protective Against Acute Myocardial Infarction R Mango, S Biocca, F del Vecchio, F Clementi, F Sangiuolo, F Amati, ... Circulation Research 97 (2), 152-158, 2005 | 138 | 2005 |
| Stem cell therapy for muscular dystrophies S Biressi, A Filareto, TA Rando The Journal of Clinical Investigation 130 (11), 5652-5664, 2020 | 70 | 2020 |
| Compound Heterozygosity for Mutations in LMNA in a Patient with a Myopathic and Lipodystrophic Mandibuloacral Dysplasia Type A Phenotype F Lombardi, F Gullotta, M Columbaro, A Filareto, M D’Adamo, A Vielle, ... The Journal of Clinical Endocrinology & Metabolism 92 (11), 4467-4471, 2007 | 64 | 2007 |
| Membrane-stabilizing copolymers confer marked protection to dystrophic skeletal muscle in vivo EM Houang, KJ Haman, A Filareto, RC Perlingeiro, FS Bates, DA Lowe, ... Molecular Therapy-Methods & Clinical Development 2, 2015 | 53 | 2015 |
| Skeletal muscle stem cells from PSC-derived teratomas have functional regenerative capacity SSK Chan, RW Arpke, A Filareto, N Xie, MP Pappas, JS Penaloza, ... Cell Stem Cell 23 (1), 74-85. e6, 2018 | 52 | 2018 |
| Identification of multipotent cytotrophoblast cells from human first trimester chorionic villi P Spitalieri, G Cortese, A Pietropolli, A Filareto, S Dolci, FG Klinger, ... Cloning and stem cells 11 (4), 535-556, 2009 | 50 | 2009 |
| IPLEX administration improves motor neuron survival and ameliorates motor functions in a severe mouse model of spinal muscular atrophy M Murdocca, A Malgieri, A Luchetti, L Saieva, G Dobrowolny, ... Molecular medicine 18, 1076-1085, 2012 | 44 | 2012 |
| Engraftment of ES-Derived Myogenic Progenitors in a Severe Mouse Model of Muscular Dystrophy RCR Perlingeiro Journal of Stem Cell Research & Therapy, 2012 | 40 | 2012 |
| In vitro restoration of functional SMN protein in human trophoblast cells affected by spinal muscular atrophy by small fragment homologous replacement F Sangiuolo, A Filareto, P Spitalieri, ML Scaldaferri, R Mango, E Bruscia, ... Human gene therapy 16 (7), 869-880, 2005 | 37 | 2005 |
| Deletion of SA β‐Gal+ cells using senolytics improves muscle regeneration in old mice CM Dungan, KA Murach, CJ Zdunek, ZJ Tang, GL Nolt, CR Brightwell, ... Aging Cell 21 (1), e13528, 2022 | 36 | 2022 |
| Cftr gene targeting in mouse embryonic stem cells mediated by Small Fragment Homologous Replacement (SFHR) F Sangiuolo, ML Scaldaferri, A Filareto, P Spitalieri, L Guerra, M Favia, ... Frontiers in bioscience: a journal and virtual library 13, 2989, 2008 | 30 | 2008 |
| Engineered DNA plasmid reduces immunity to dystrophin while improving muscle force in a model of gene therapy of Duchenne dystrophy PP Ho, LJ Lahey, F Mourkioti, PE Kraft, A Filareto, M Brandt, ... Proceedings of the National Academy of Sciences 115 (39), E9182-E9191, 2018 | 21 | 2018 |
| Pax3-induced expansion enables the genetic correction of dystrophic satellite cells A Filareto, F Rinaldi, RW Arpke, R Darabi, JJ Belanto, EA Toso, AZ Miller, ... Skeletal Muscle 5, 1-11, 2015 | 20 | 2015 |
| Pharmacological TRPC6 inhibition improves survival and muscle function in mice with Duchenne muscular dystrophy. KD Lin B., Shin J., Jeffreys W, Wang N., Lukban C., Moorer M., Velarde E ... JCI insight, 2022 | 10 | 2022 |
| Monitoring disease activity noninvasively in the mdx model of Duchenne muscular dystrophy A Filareto, K Maguire-Nguyen, Q Gan, G Aldanondo, L Machado, ... Proceedings of the National Academy of Sciences 115 (30), 7741-7746, 2018 | 7 | 2018 |
| Small fragment homologous replacement: evaluation of factors influencing modification efficiency in an eukaryotic assay system A Luchetti, A Filareto, M Sanchez, G Ferraguti, M Lucarelli, G Novelli, ... Plos one 7 (2), e30851, 2012 | 7 | 2012 |
| Prenatal diagnosis of spinal muscular atrophy with respiratory distress (SMARD1) in a twin pregnancy F Sangiuolo, A Filareto, E Giardina, AM Nardone, G Pilu, A Pietropolli, ... Prenatal Diagnosis: Published in Affiliation With the International Society …, 2004 | 6 | 2004 |
| An ex vivo gene therapy approach to treat muscular dystrophy using inducible pluripotent stem cells. Nat Commun. 2013; 4: 1549 A Filareto, S Parker, R Darabi, L Borges, M Iacovino, T Schaaf | 5 | |
Luciene BorgesPrincipal Scientist, Boehringer IngelheimVerified email at stanford.edu
